| A | B | C | |
|---|---|---|---|
| 1 | Main | ||
| 2 | Brand | Onpattro | |
| 3 | Generic | patisiran | |
| 4 | Indication | ATTR Amyloidosis. Neuropathy & Cardiomyopathy. | |
| 5 | Clinical Trials | ||
| 6 | Phase III "APOLLO-B" n=360 ATTR with cardiomyopathy | ||
| 7 | 6MW PE met at 12 months: +14.7m, p=0.0162 | ||
| 8 | '-8.15 for patisiran, -21.345 for placebo | ||
| 9 | Initially presented at ISA, press release 8/2022; HFSA 10/2022 | ||
| 10 | 0.3mg/kg IV q3w | ||
| 11 | MACE HR=0.839 p=NS |